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Allogeneic hematopoietic SCT as treatment option for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE): a consensus conference proposal for a standardized approach

Record type: Article

Allogeneic hematopoietic SCT (HSCT) has been proposed as a treatment for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE). HSCT has been performed in nine patients using different protocols with varying success. Based on this preliminary experience, participants of the first consensus conference propose a common approach to allogeneic HSCT in MNGIE. Standardization of the transplant protocol and the clinical and biochemical assessments will allow evaluation of the safety and efficacy of HSCT as well as optimization of therapy for patients with MNGIE.

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Citation

Halter, J., Schüpbach, W.M.M., Casali, C., Elhasid, R., Fay, K., Hammans, S., Illa, I., Kappeler, L., Krähenbühl, S., Lehmann, T., Mandel, H., Marti, R., Mattle, H., Orchard, K., Savage, D., Sue, C. M., Valcarcel, D., Gratwohl, A. and Hirano, M. (2011) Allogeneic hematopoietic SCT as treatment option for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE): a consensus conference proposal for a standardized approach Bone Marrow Transplantation, 46, (3), pp. 330-337. (doi:10.1038/bmt.2010.100).

More information

Published date: May 2011
Organisations: Cancer Sciences

Identifiers

Local EPrints ID: 341438
URI: http://eprints.soton.ac.uk/id/eprint/341438
ISSN: 0268-3369
PURE UUID: ca71396e-4cf0-4a43-b746-ac5b98a3a46f
ORCID for K. Orchard: ORCID iD orcid.org/0000-0003-2276-3925

Catalogue record

Date deposited: 25 Jul 2012 10:48
Last modified: 18 Jul 2017 05:36

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Contributors

Author: J. Halter
Author: W.M.M. Schüpbach
Author: C. Casali
Author: R. Elhasid
Author: K. Fay
Author: S. Hammans
Author: I. Illa
Author: L. Kappeler
Author: S. Krähenbühl
Author: T. Lehmann
Author: H. Mandel
Author: R. Marti
Author: H. Mattle
Author: K. Orchard ORCID iD
Author: D. Savage
Author: C. M. Sue
Author: D. Valcarcel
Author: A. Gratwohl
Author: M. Hirano

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