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A phase 2/3 multicenter, randomized, open-label study to compare the efficacy and safety of Lenalidomide versus investigator's choice in patients with relapsed or refractory diffuse large B-Cell lymphoma

A phase 2/3 multicenter, randomized, open-label study to compare the efficacy and safety of Lenalidomide versus investigator's choice in patients with relapsed or refractory diffuse large B-Cell lymphoma
A phase 2/3 multicenter, randomized, open-label study to compare the efficacy and safety of Lenalidomide versus investigator's choice in patients with relapsed or refractory diffuse large B-Cell lymphoma

Purpose: Randomized, multicenter, open-label, phase 2/3 trial investigating lenalidomide versus investigator's choice (IC) in relapsed/refractory diffuse large B-cell lymphoma (DLBCL).Experimental Design: Patients with DLBCL who received ≥2 prior therapies were stratified by DLBCL subtype [germinal center B-cell (GCB) vs. non-GCB; determined by immunohistochemistry (IHC)] and then randomized 1:1 to lenalidomide (25 mg/day, 21 days of 28-day cycle) or IC (gemcitabine, rituximab, etoposide, or oxaliplatin). Crossover to lenalidomide was permitted for IC-treated patients with radiologically confirmed progressive disease. The primary endpoint was overall response rate (ORR). Progression-free survival (PFS), overall survival, and subtype analysis [GCB vs. activated B-cell (ABC)] using gene expression profiling (GEP) were exploratory endpoints.Results: Stage 1: 102 DLBCL patients (by IHC: non-GCB, n = 54; GCB, n = 48) received ≥1 dose of lenalidomide or IC. Hematologic treatment-emergent adverse events with lenalidomide versus IC included neutropenia (42.6%; 36.4%), anemia (33.3%; 47.3%), thrombocytopenia (24.1%; 43.6%), and leukopenia (5.6%; 12.7%), respectively. Overall, lenalidomide-treated patients had an ORR of 27.5% versus 11.8% in IC (ORRs were similar regardless of IHC-defined DLBCL subtype). Median PFS was increased in patients receiving lenalidomide (13.6 weeks) versus IC (7.9 weeks; P = 0.041), with greater improvements in non-GCB patients (15.1 vs. 7.1 weeks, respectively; P = 0.021) compared with GCB (10.1 vs. 9.0 weeks, respectively; P = 0.550).Conclusions: The clinical benefit of lenalidomide monotherapy in DLBCL patients was more evident in the non-GCB subtype. Exploratory analyses suggest that this preferential benefit was more pronounced in the GEP-defined ABC population, demonstrating a need for additional studies of lenalidomide in DLBCL using GEP subtyping. Clin Cancer Res; 23(15); 4127-37. ©2017 AACR.

Journal Article
1078-0432
4127-4137
Czuczman, Myron S.
78414cc5-ea96-498a-8c58-146d3600e96c
Trněný, Marek
dba5f989-8e4e-4c17-81fb-87d62a7515fc
Davies, Andrew
0fe6a40a-10d1-4ade-a7e6-d1dceb2470af
Rule, Simon
cc835ff1-f9a5-47a4-b815-76e516e157e7
Linton, Kim M.
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Wagner-Johnston, Nina
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Gascoyne, Randy D.
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Slack, Graham W
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Brousset, Pierre
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Eberhard, David A.
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Hernandez-Ilizaliturri, Francisco J.
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Salles, Gilles
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Witzig, Thomas E.
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Zinzani, Pier Luigi
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Wright, George W.
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Staudt, Louis M.
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Yang, Yandan
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Williams, P. Mickey
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Lih, Chih-Jian
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Russo, Jacqueline
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Thakurta, Anjan
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Hagner, Patrick
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Fustier, Pierre
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Song, Dale
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Lewis, Ian D.
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Czuczman, Myron S.
78414cc5-ea96-498a-8c58-146d3600e96c
Trněný, Marek
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Davies, Andrew
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Rule, Simon
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Linton, Kim M.
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Wagner-Johnston, Nina
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Gascoyne, Randy D.
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Slack, Graham W
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Brousset, Pierre
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Eberhard, David A.
950879cb-fc76-4d37-ac3d-0adb012c3602
Hernandez-Ilizaliturri, Francisco J.
5eee23c0-a03f-43ec-aebe-5cefc3799bc7
Salles, Gilles
2101b738-f4ff-4243-b8d0-0c2fee7454bd
Witzig, Thomas E.
5f4668d1-2866-4fb8-8769-3407b8140851
Zinzani, Pier Luigi
c8a817bb-0f54-4bde-90b2-d3339ed8fff5
Wright, George W.
bf161dfa-bd4f-4d6e-b441-e2e80125b056
Staudt, Louis M.
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Yang, Yandan
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Williams, P. Mickey
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Lih, Chih-Jian
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Russo, Jacqueline
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Thakurta, Anjan
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Hagner, Patrick
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Fustier, Pierre
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Song, Dale
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Lewis, Ian D.
3582e9d6-3055-44d6-9b0a-6ab71d0d9d5d

Czuczman, Myron S., Trněný, Marek, Davies, Andrew, Rule, Simon, Linton, Kim M., Wagner-Johnston, Nina, Gascoyne, Randy D., Slack, Graham W, Brousset, Pierre, Eberhard, David A., Hernandez-Ilizaliturri, Francisco J., Salles, Gilles, Witzig, Thomas E., Zinzani, Pier Luigi, Wright, George W., Staudt, Louis M., Yang, Yandan, Williams, P. Mickey, Lih, Chih-Jian, Russo, Jacqueline, Thakurta, Anjan, Hagner, Patrick, Fustier, Pierre, Song, Dale and Lewis, Ian D. (2017) A phase 2/3 multicenter, randomized, open-label study to compare the efficacy and safety of Lenalidomide versus investigator's choice in patients with relapsed or refractory diffuse large B-Cell lymphoma. Clinical Cancer Research, 23 (15), 4127-4137. (doi:10.1158/1078-0432.CCR-16-2818).

Record type: Article

Abstract

Purpose: Randomized, multicenter, open-label, phase 2/3 trial investigating lenalidomide versus investigator's choice (IC) in relapsed/refractory diffuse large B-cell lymphoma (DLBCL).Experimental Design: Patients with DLBCL who received ≥2 prior therapies were stratified by DLBCL subtype [germinal center B-cell (GCB) vs. non-GCB; determined by immunohistochemistry (IHC)] and then randomized 1:1 to lenalidomide (25 mg/day, 21 days of 28-day cycle) or IC (gemcitabine, rituximab, etoposide, or oxaliplatin). Crossover to lenalidomide was permitted for IC-treated patients with radiologically confirmed progressive disease. The primary endpoint was overall response rate (ORR). Progression-free survival (PFS), overall survival, and subtype analysis [GCB vs. activated B-cell (ABC)] using gene expression profiling (GEP) were exploratory endpoints.Results: Stage 1: 102 DLBCL patients (by IHC: non-GCB, n = 54; GCB, n = 48) received ≥1 dose of lenalidomide or IC. Hematologic treatment-emergent adverse events with lenalidomide versus IC included neutropenia (42.6%; 36.4%), anemia (33.3%; 47.3%), thrombocytopenia (24.1%; 43.6%), and leukopenia (5.6%; 12.7%), respectively. Overall, lenalidomide-treated patients had an ORR of 27.5% versus 11.8% in IC (ORRs were similar regardless of IHC-defined DLBCL subtype). Median PFS was increased in patients receiving lenalidomide (13.6 weeks) versus IC (7.9 weeks; P = 0.041), with greater improvements in non-GCB patients (15.1 vs. 7.1 weeks, respectively; P = 0.021) compared with GCB (10.1 vs. 9.0 weeks, respectively; P = 0.550).Conclusions: The clinical benefit of lenalidomide monotherapy in DLBCL patients was more evident in the non-GCB subtype. Exploratory analyses suggest that this preferential benefit was more pronounced in the GEP-defined ABC population, demonstrating a need for additional studies of lenalidomide in DLBCL using GEP subtyping. Clin Cancer Res; 23(15); 4127-37. ©2017 AACR.

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More information

Accepted/In Press date: 31 March 2017
e-pub ahead of print date: 5 April 2017
Published date: 1 August 2017
Keywords: Journal Article

Identifiers

Local EPrints ID: 417970
URI: http://eprints.soton.ac.uk/id/eprint/417970
ISSN: 1078-0432
PURE UUID: e48043e5-5b03-42fd-b209-aa591cb17ac2
ORCID for Andrew Davies: ORCID iD orcid.org/0000-0002-7517-6938

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Date deposited: 19 Feb 2018 17:31
Last modified: 16 Mar 2024 03:58

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Contributors

Author: Myron S. Czuczman
Author: Marek Trněný
Author: Andrew Davies ORCID iD
Author: Simon Rule
Author: Kim M. Linton
Author: Nina Wagner-Johnston
Author: Randy D. Gascoyne
Author: Graham W Slack
Author: Pierre Brousset
Author: David A. Eberhard
Author: Francisco J. Hernandez-Ilizaliturri
Author: Gilles Salles
Author: Thomas E. Witzig
Author: Pier Luigi Zinzani
Author: George W. Wright
Author: Louis M. Staudt
Author: Yandan Yang
Author: P. Mickey Williams
Author: Chih-Jian Lih
Author: Jacqueline Russo
Author: Anjan Thakurta
Author: Patrick Hagner
Author: Pierre Fustier
Author: Dale Song
Author: Ian D. Lewis

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