Avalglucosidase alfa for treating Pompe disease
Avalglucosidase alfa for treating Pompe disease
This report is a critique of the company’s submission (CS) to NICE from Sanofi on the
clinical effectiveness and cost effectiveness of AVAL for treating Pompe Disease. It identifies the strengths and weakness of the CS.
National Institute for Health and Care Research
Ribeiro, Ines
2fd1901b-61bd-4ad5-81b3-a3f8145ec144
Maund, Emma
c9733167-eafe-44e5-b418-5ace79161402
Cooper, Keith
ea064f58-d71d-404a-bcf3-49d243b8825b
Pickett, Karen
1bac9d88-da29-4a3e-9fd2-e469f129f963
Takahashi, Marcia Tomie
fa084efd-dc46-4325-8fc9-d3f6d1f8b5d0
Scott, David Alexander
19b5fd34-9974-4ae4-8be0-27a693639e20
Shepherd, Jonathan
dfbca97a-9307-4eee-bdf7-e27bcb02bc67
2022
Ribeiro, Ines
2fd1901b-61bd-4ad5-81b3-a3f8145ec144
Maund, Emma
c9733167-eafe-44e5-b418-5ace79161402
Cooper, Keith
ea064f58-d71d-404a-bcf3-49d243b8825b
Pickett, Karen
1bac9d88-da29-4a3e-9fd2-e469f129f963
Takahashi, Marcia Tomie
fa084efd-dc46-4325-8fc9-d3f6d1f8b5d0
Scott, David Alexander
19b5fd34-9974-4ae4-8be0-27a693639e20
Shepherd, Jonathan
dfbca97a-9307-4eee-bdf7-e27bcb02bc67
Ribeiro, Ines, Maund, Emma, Cooper, Keith, Pickett, Karen, Takahashi, Marcia Tomie, Scott, David Alexander and Shepherd, Jonathan
(2022)
Avalglucosidase alfa for treating Pompe disease
(Health Technology Assessment, NIHR 135193)
National Institute for Health and Care Research
164pp.
Record type:
Monograph
(Project Report)
Abstract
This report is a critique of the company’s submission (CS) to NICE from Sanofi on the
clinical effectiveness and cost effectiveness of AVAL for treating Pompe Disease. It identifies the strengths and weakness of the CS.
Text
ERG report - avalglucosidase alfa
- Version of Record
Available under License Other.
More information
Published date: 2022
Identifiers
Local EPrints ID: 471449
URI: http://eprints.soton.ac.uk/id/eprint/471449
PURE UUID: 7b5cb419-f5a8-4248-827c-69ca30d5f34e
Catalogue record
Date deposited: 08 Nov 2022 18:32
Last modified: 11 Sep 2024 02:31
Export record
Contributors
Author:
David Alexander Scott
Download statistics
Downloads from ePrints over the past year. Other digital versions may also be available to download e.g. from the publisher's website.
View more statistics