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The impact of liver transplantation on the phenotype of primary biliary cirrhosis patients in the UK-PBC cohort

The impact of liver transplantation on the phenotype of primary biliary cirrhosis patients in the UK-PBC cohort
The impact of liver transplantation on the phenotype of primary biliary cirrhosis patients in the UK-PBC cohort

BACKGROUND & AIMS: Liver transplantation improves survival in end-stage primary biliary cirrhosis (PBC), but the benefit for systemic symptoms including fatigue is less clear. The aim of this study was to utilise the comprehensive UK-PBC Research Cohort, including 380 post-transplant patients and 2300 non-transplanted patients, to answer key questions regarding transplantation for PBC.

METHODS: Cross-sectional study of post-transplant PBC patients and case-matched non-transplanted patients. Detailed clinical information was collected, together with patient systemic symptom impact data using validated assessment tools.

RESULTS: Over 25% of patients in the transplant cohort were grafted within 2 years of PBC diagnosis suggesting advanced disease at presentation. Transplanted patients were significantly younger at presentation than non-transplanted (mean 7 years) and >35% of all patients in the UK-PBC cohort who presented under 50 years had already undergone liver transplantation at the study censor point (>50% were treatment failures (post-transplant or unresponsive to UDCA)). Systemic symptom severity (fatigue and cognitive symptoms) was identical in female post-transplant patients and matched non-transplanted controls and unrelated to disease recurrence or immunosuppression type. In males, symptoms were worse in transplanted than in non-transplanted patients.

CONCLUSIONS: Age at presentation is a major risk factor for progression to transplant (as well as UDCA non-response) in PBC. Although both confirmatory longitudinal studies, and studies utilising objective as well as subjective measures of function, are needed if we are to address the question definitively, we found no evidence of improved systemic symptoms after liver transplantation in PBC and patients should be advised accordingly. Consideration needs to be given to enhancing rehabilitation approaches to improve function and life quality after liver transplant for PBC.

Adult, Age Factors, Aged, Cohort Studies, Cross-Sectional Studies, Fatigue/etiology, Female, Humans, Liver Cirrhosis, Biliary/physiopathology, Liver Transplantation/adverse effects, Male, Middle Aged, Phenotype, Quality of Life, Risk Factors, Sex Factors, United Kingdom
0168-8278
67-73
Pells, Greta
f3c97d0c-ccbd-45b9-be1a-2fce7823d4dd
Mells, George F
63e52765-505a-4ae6-af08-484cf4c46059
Carbone, Marco
2a402972-c971-4f89-94bc-a415f1ad0e8a
Newton, Julia L
7075a4eb-7985-44fb-b02c-aae9c1c30004
Bathgate, Andrew J
8534fc1e-46d3-4e9e-9ef5-ddba2778d1f8
Burroughs, Andrew K
531a7a81-77ef-4188-ab96-352ea7412f50
Heneghan, Michael A
02ca4e3b-ddee-4d6d-90fa-6880c05bf12c
Neuberger, James M
5767dd7d-609d-41e5-85e9-8d504063a912
Day, Darren B
fb3fa707-1d1c-4bc8-9388-9c49f7399257
Ducker, Samantha J
d7c2c244-827c-4537-a68f-273acd90e3f2
Sandford, Richard N
1f9a5d2b-d14a-43b3-b326-fa9ab17b406f
Alexander, Graeme J
3373aaa7-0249-4edd-b88f-a63677f32bba
Jones, David E J
b8f3e32c-d537-445a-a1e4-7436f472e160
UK-PBC Consortium
Pells, Greta
f3c97d0c-ccbd-45b9-be1a-2fce7823d4dd
Mells, George F
63e52765-505a-4ae6-af08-484cf4c46059
Carbone, Marco
2a402972-c971-4f89-94bc-a415f1ad0e8a
Newton, Julia L
7075a4eb-7985-44fb-b02c-aae9c1c30004
Bathgate, Andrew J
8534fc1e-46d3-4e9e-9ef5-ddba2778d1f8
Burroughs, Andrew K
531a7a81-77ef-4188-ab96-352ea7412f50
Heneghan, Michael A
02ca4e3b-ddee-4d6d-90fa-6880c05bf12c
Neuberger, James M
5767dd7d-609d-41e5-85e9-8d504063a912
Day, Darren B
fb3fa707-1d1c-4bc8-9388-9c49f7399257
Ducker, Samantha J
d7c2c244-827c-4537-a68f-273acd90e3f2
Sandford, Richard N
1f9a5d2b-d14a-43b3-b326-fa9ab17b406f
Alexander, Graeme J
3373aaa7-0249-4edd-b88f-a63677f32bba
Jones, David E J
b8f3e32c-d537-445a-a1e4-7436f472e160

UK-PBC Consortium (2013) The impact of liver transplantation on the phenotype of primary biliary cirrhosis patients in the UK-PBC cohort. Journal of Hepatology, 59 (1), 67-73. (doi:10.1016/j.jhep.2013.02.019).

Record type: Article

Abstract

BACKGROUND & AIMS: Liver transplantation improves survival in end-stage primary biliary cirrhosis (PBC), but the benefit for systemic symptoms including fatigue is less clear. The aim of this study was to utilise the comprehensive UK-PBC Research Cohort, including 380 post-transplant patients and 2300 non-transplanted patients, to answer key questions regarding transplantation for PBC.

METHODS: Cross-sectional study of post-transplant PBC patients and case-matched non-transplanted patients. Detailed clinical information was collected, together with patient systemic symptom impact data using validated assessment tools.

RESULTS: Over 25% of patients in the transplant cohort were grafted within 2 years of PBC diagnosis suggesting advanced disease at presentation. Transplanted patients were significantly younger at presentation than non-transplanted (mean 7 years) and >35% of all patients in the UK-PBC cohort who presented under 50 years had already undergone liver transplantation at the study censor point (>50% were treatment failures (post-transplant or unresponsive to UDCA)). Systemic symptom severity (fatigue and cognitive symptoms) was identical in female post-transplant patients and matched non-transplanted controls and unrelated to disease recurrence or immunosuppression type. In males, symptoms were worse in transplanted than in non-transplanted patients.

CONCLUSIONS: Age at presentation is a major risk factor for progression to transplant (as well as UDCA non-response) in PBC. Although both confirmatory longitudinal studies, and studies utilising objective as well as subjective measures of function, are needed if we are to address the question definitively, we found no evidence of improved systemic symptoms after liver transplantation in PBC and patients should be advised accordingly. Consideration needs to be given to enhancing rehabilitation approaches to improve function and life quality after liver transplant for PBC.

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More information

Accepted/In Press date: 25 February 2013
e-pub ahead of print date: 4 March 2013
Published date: 1 July 2013
Additional Information: Copyright © 2013. Published by Elsevier B.V.
Keywords: Adult, Age Factors, Aged, Cohort Studies, Cross-Sectional Studies, Fatigue/etiology, Female, Humans, Liver Cirrhosis, Biliary/physiopathology, Liver Transplantation/adverse effects, Male, Middle Aged, Phenotype, Quality of Life, Risk Factors, Sex Factors, United Kingdom

Identifiers

Local EPrints ID: 479666
URI: http://eprints.soton.ac.uk/id/eprint/479666
ISSN: 0168-8278
PURE UUID: 45d4e00c-b24e-404a-ab69-4d0c31d6bff6
ORCID for David E J Jones: ORCID iD orcid.org/0000-0002-0117-7567

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Date deposited: 26 Jul 2023 16:45
Last modified: 17 Mar 2024 02:48

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Contributors

Author: Greta Pells
Author: George F Mells
Author: Marco Carbone
Author: Julia L Newton
Author: Andrew J Bathgate
Author: Andrew K Burroughs
Author: Michael A Heneghan
Author: James M Neuberger
Author: Darren B Day
Author: Samantha J Ducker
Author: Richard N Sandford
Author: Graeme J Alexander
Author: David E J Jones ORCID iD
Corporate Author: UK-PBC Consortium

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