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Consensus statement for protocols of factorial randomized trials: extension of the SPIRIT 2013 statement

Consensus statement for protocols of factorial randomized trials: extension of the SPIRIT 2013 statement
Consensus statement for protocols of factorial randomized trials: extension of the SPIRIT 2013 statement
Importance: trial protocols outline a trial’s objectives as well as the methods (design, conduct, and analysis) that will be used to meet those objectives, and transparent reporting of trial protocols ensures objectives are clear and facilitates appraisal regarding the suitability of study methods. Factorial trials, in which 2 or more interventions are assessed in the same set of participants, have unique methodological considerations. However, no extension of the Standard Protocol Items: Recommendations for Interventional Trials (SPIRIT) 2013 Statement, which provides guidance on reporting of trial protocols, for factorial trials is available.

Objective: to develop a consensus-based extension to the SPIRIT 2013 Statement for factorial trials.

Evidence review: the SPIRIT extension for factorial trials was developed using the Enhancing the Quality and Transparency of Health Research (EQUATOR) methodological framework. First, a list of reporting recommendations was generated using a scoping review of methodological articles identified using a MEDLINE search (inception to May 2019), which was supplemented with relevant articles from the personal collections of the authors. Second, a 3-round Delphi survey (January to June 2022, completed by 104 panelists from 14 countries) was conducted to assess the importance of items and identify additional recommendations. Third, a hybrid consensus meeting was held, attended by 15 panelists to finalize selection and wording of the checklist.

Findings: this SPIRIT extension for factorial trials modified 9 of the 33 items in the SPIRIT 2013 checklist. Key reporting recommendations were that the rationale for using a factorial design should be provided, including whether an interaction is hypothesized; the treatment groups that will form the main comparisons should be identified; and statistical methods for each main comparison should be provided, including how interactions will be assessed.

Conclusions and relevance: in this consensus statement, 9 factorial-specific items were provided that should be addressed in all protocols of factorial trials to increase the trial’s utility and transparency.
2574-3805
Kahan, Brennan C.
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Hall, Sophie S.
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Beller, Elaine M.
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Birchenall, Megan
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Elbourne, Diana
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Juszczak, Edmund
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Little, Paul
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Fletcher, John
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Golub, Robert M.
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Goulao, Beatriz
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Hopewell, Sally
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Islam, Nazrul
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Zwarenstein, Merrick
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Chan, An-Wen
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Montgomery, Alan A.
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Kahan, Brennan C.
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Hall, Sophie S.
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Beller, Elaine M.
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Birchenall, Megan
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Elbourne, Diana
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Juszczak, Edmund
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Little, Paul
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Fletcher, John
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Golub, Robert M.
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Goulao, Beatriz
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Hopewell, Sally
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Islam, Nazrul
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Zwarenstein, Merrick
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Chan, An-Wen
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Montgomery, Alan A.
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Kahan, Brennan C., Hall, Sophie S., Beller, Elaine M., Birchenall, Megan, Elbourne, Diana, Juszczak, Edmund, Little, Paul, Fletcher, John, Golub, Robert M., Goulao, Beatriz, Hopewell, Sally, Islam, Nazrul, Zwarenstein, Merrick, Chan, An-Wen and Montgomery, Alan A. (2023) Consensus statement for protocols of factorial randomized trials: extension of the SPIRIT 2013 statement. JAMA Network Open, 6 (12), [e2346121]. (doi:10.1001/jamanetworkopen.2023.46121).

Record type: Article

Abstract

Importance: trial protocols outline a trial’s objectives as well as the methods (design, conduct, and analysis) that will be used to meet those objectives, and transparent reporting of trial protocols ensures objectives are clear and facilitates appraisal regarding the suitability of study methods. Factorial trials, in which 2 or more interventions are assessed in the same set of participants, have unique methodological considerations. However, no extension of the Standard Protocol Items: Recommendations for Interventional Trials (SPIRIT) 2013 Statement, which provides guidance on reporting of trial protocols, for factorial trials is available.

Objective: to develop a consensus-based extension to the SPIRIT 2013 Statement for factorial trials.

Evidence review: the SPIRIT extension for factorial trials was developed using the Enhancing the Quality and Transparency of Health Research (EQUATOR) methodological framework. First, a list of reporting recommendations was generated using a scoping review of methodological articles identified using a MEDLINE search (inception to May 2019), which was supplemented with relevant articles from the personal collections of the authors. Second, a 3-round Delphi survey (January to June 2022, completed by 104 panelists from 14 countries) was conducted to assess the importance of items and identify additional recommendations. Third, a hybrid consensus meeting was held, attended by 15 panelists to finalize selection and wording of the checklist.

Findings: this SPIRIT extension for factorial trials modified 9 of the 33 items in the SPIRIT 2013 checklist. Key reporting recommendations were that the rationale for using a factorial design should be provided, including whether an interaction is hypothesized; the treatment groups that will form the main comparisons should be identified; and statistical methods for each main comparison should be provided, including how interactions will be assessed.

Conclusions and relevance: in this consensus statement, 9 factorial-specific items were provided that should be addressed in all protocols of factorial trials to increase the trial’s utility and transparency.

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Published date: 5 December 2023
Additional Information: Funding/Support: This work was supported by the Medical Research Council [grant number MR/V020803/1].

Identifiers

Local EPrints ID: 486816
URI: http://eprints.soton.ac.uk/id/eprint/486816
ISSN: 2574-3805
PURE UUID: 769f5faf-47d4-40dd-8a28-1993aeba14c2
ORCID for Paul Little: ORCID iD orcid.org/0000-0003-3664-1873
ORCID for Nazrul Islam: ORCID iD orcid.org/0000-0003-3982-4325

Catalogue record

Date deposited: 06 Feb 2024 17:47
Last modified: 12 Jul 2024 02:12

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Contributors

Author: Brennan C. Kahan
Author: Sophie S. Hall
Author: Elaine M. Beller
Author: Megan Birchenall
Author: Diana Elbourne
Author: Edmund Juszczak
Author: Paul Little ORCID iD
Author: John Fletcher
Author: Robert M. Golub
Author: Beatriz Goulao
Author: Sally Hopewell
Author: Nazrul Islam ORCID iD
Author: Merrick Zwarenstein
Author: An-Wen Chan
Author: Alan A. Montgomery

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