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Whole-body hypothermia in mild neonatal encephalopathy: protocol for a multicentre phase III randomised controlled trial

Whole-body hypothermia in mild neonatal encephalopathy: protocol for a multicentre phase III randomised controlled trial
Whole-body hypothermia in mild neonatal encephalopathy: protocol for a multicentre phase III randomised controlled trial

BACKGROUND: Mild hypoxic ischemic encephalopathy is associated with sub optimal cognition and learning difficulties at school age. Although whole-body hypothermia reduces death and disability after moderate or severe encephalopathy in high-income countries, the safety and efficacy of hypothermia in mild encephalopathy is not known. The cooling in mild encephalopathy (COMET) trial will examine if whole-body hypothermia improves cognitive development of neonates with mild encephalopathy.

METHODS: The COMET trial is a phase III multicentre open label two-arm randomised controlled trial with masked outcome assessments. A total of 426 neonates with mild encephalopathy will be recruited from 50 to 60 NHS hospitals over 2 ½ years following parental consent. The neonates will be randomised to 72 h of whole-body hypothermia (33.5 ± 0.5 C) or normothermia (37.0 ± 0.5 C) within six hours or age. Prior to the recruitment front line clinical staff will be trained and certified on expanded modified Sarnat staging for encephalopathy. The neurological assessment of all screened and recruited cases will be video recorded and centrally assessed for quality assurance. If recruitment occurs at a non-cooling centre, neonates in both arms will be transferred to a cooling centre for continued care, after randomisation. All neonates will have continuous amplitude integrated electroencephalography (aEEG) at least for the first 48 h to monitor for seizures. Predefined safety outcomes will be documented, and data collected to assess resource utilization of health care. A central team masked to trial group allocation will assess neurodevelopmental outcomes at 2 years of age. The primary outcome is mean difference in composite cognitive scores on Bayley scales of Infant and Toddler development 4th Edition.

DISCUSSION: The COMET trial will establish the safety and efficacy of whole-body hypothermia for mild hypoxic ischaemic encephalopathy and inform national and international guidelines in high income countries. It will also provide an economic assessment of whole-body hypothermia therapy for mild encephalopathy in the NHS on cost-effectiveness grounds.

TRIAL REGISTRATION NUMBER: NCT05889507 June 5, 2023.

Clinical Trials, Phase III as Topic, Humans, Hypothermia, Induced/methods, Hypoxia-Ischemia, Brain/therapy, Infant, Newborn, Multicenter Studies as Topic, Randomized Controlled Trials as Topic
1471-2431
Garegrat, Reema
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Montaldo, Paolo
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Burgod, Constance
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Pant, Stuti
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Mazlan, Munirah
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Palanisami, Balamurugan
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Chakkarapani, Ela
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Woolfall, Kerry
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Johnson, Samantha
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Grant, Patricia Ellen
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Land, Sarah
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Mahmoud, Mariam
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Brady, Tony
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Cornelius, Victoria
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Adams, Eleri
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Dorling, Jon
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Aladangadi, Narendra
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Fleming, Paul
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Pressler, Ronit
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Shennan, Andrew
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Petrou, Stavros
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Soe, Aung
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Basset, Paul
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Shankaran, Seetha
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Thayyil, Sudhin
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Garegrat, Reema
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Montaldo, Paolo
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Burgod, Constance
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Pant, Stuti
07ce2e3f-dd1d-4f5b-b102-6e45dc40db2b
Mazlan, Munirah
53496cd4-a06a-4d83-a08d-c6113f9fe466
Palanisami, Balamurugan
a32c5e30-c014-4f9e-a19b-202cc631e8e5
Chakkarapani, Ela
9a5809d8-7c02-48d7-856e-bd04b214e062
Woolfall, Kerry
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Johnson, Samantha
089534c4-0108-484b-9999-a634613afe10
Grant, Patricia Ellen
d54baf44-b9c0-4f33-95d9-cccdb654c753
Land, Sarah
87bd5d29-6b44-4c9a-8410-acab5a29f065
Mahmoud, Mariam
fe52eae2-baae-4c39-afd4-6e4c45a144da
Brady, Tony
82577728-d666-442a-8bd1-e756be5020e0
Cornelius, Victoria
9221c843-6ee8-40af-8759-f2c0751ac958
Adams, Eleri
f4f301c6-5390-4539-aa11-5bd87a8623f4
Dorling, Jon
e55dcb9a-a798-41a1-8753-9e9ff8aab630
Aladangadi, Narendra
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Fleming, Paul
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Pressler, Ronit
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Shennan, Andrew
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Petrou, Stavros
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Soe, Aung
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Basset, Paul
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Shankaran, Seetha
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Thayyil, Sudhin
878f7084-dd55-4e30-97f3-565a74ae6dc1

Garegrat, Reema, Montaldo, Paolo, Burgod, Constance, Pant, Stuti, Mazlan, Munirah, Palanisami, Balamurugan, Chakkarapani, Ela, Woolfall, Kerry, Johnson, Samantha, Grant, Patricia Ellen, Land, Sarah, Mahmoud, Mariam, Brady, Tony, Cornelius, Victoria, Adams, Eleri, Dorling, Jon, Aladangadi, Narendra, Fleming, Paul, Pressler, Ronit, Shennan, Andrew, Petrou, Stavros, Soe, Aung, Basset, Paul, Shankaran, Seetha and Thayyil, Sudhin (2024) Whole-body hypothermia in mild neonatal encephalopathy: protocol for a multicentre phase III randomised controlled trial. BMC Pediatrics, 24 (1), [460]. (doi:10.1186/s12887-024-04935-4).

Record type: Article

Abstract

BACKGROUND: Mild hypoxic ischemic encephalopathy is associated with sub optimal cognition and learning difficulties at school age. Although whole-body hypothermia reduces death and disability after moderate or severe encephalopathy in high-income countries, the safety and efficacy of hypothermia in mild encephalopathy is not known. The cooling in mild encephalopathy (COMET) trial will examine if whole-body hypothermia improves cognitive development of neonates with mild encephalopathy.

METHODS: The COMET trial is a phase III multicentre open label two-arm randomised controlled trial with masked outcome assessments. A total of 426 neonates with mild encephalopathy will be recruited from 50 to 60 NHS hospitals over 2 ½ years following parental consent. The neonates will be randomised to 72 h of whole-body hypothermia (33.5 ± 0.5 C) or normothermia (37.0 ± 0.5 C) within six hours or age. Prior to the recruitment front line clinical staff will be trained and certified on expanded modified Sarnat staging for encephalopathy. The neurological assessment of all screened and recruited cases will be video recorded and centrally assessed for quality assurance. If recruitment occurs at a non-cooling centre, neonates in both arms will be transferred to a cooling centre for continued care, after randomisation. All neonates will have continuous amplitude integrated electroencephalography (aEEG) at least for the first 48 h to monitor for seizures. Predefined safety outcomes will be documented, and data collected to assess resource utilization of health care. A central team masked to trial group allocation will assess neurodevelopmental outcomes at 2 years of age. The primary outcome is mean difference in composite cognitive scores on Bayley scales of Infant and Toddler development 4th Edition.

DISCUSSION: The COMET trial will establish the safety and efficacy of whole-body hypothermia for mild hypoxic ischaemic encephalopathy and inform national and international guidelines in high income countries. It will also provide an economic assessment of whole-body hypothermia therapy for mild encephalopathy in the NHS on cost-effectiveness grounds.

TRIAL REGISTRATION NUMBER: NCT05889507 June 5, 2023.

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s12887-024-04935-4 - Version of Record
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More information

Accepted/In Press date: 8 July 2024
Published date: 18 July 2024
Additional Information: © 2024. The Author(s).
Keywords: Clinical Trials, Phase III as Topic, Humans, Hypothermia, Induced/methods, Hypoxia-Ischemia, Brain/therapy, Infant, Newborn, Multicenter Studies as Topic, Randomized Controlled Trials as Topic

Identifiers

Local EPrints ID: 492942
URI: http://eprints.soton.ac.uk/id/eprint/492942
ISSN: 1471-2431
PURE UUID: 28a9b91e-7106-4378-bf9d-59d92ede8ae5
ORCID for Jon Dorling: ORCID iD orcid.org/0000-0002-1691-3221

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Date deposited: 21 Aug 2024 16:36
Last modified: 22 Aug 2024 02:10

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Contributors

Author: Reema Garegrat
Author: Paolo Montaldo
Author: Constance Burgod
Author: Stuti Pant
Author: Munirah Mazlan
Author: Balamurugan Palanisami
Author: Ela Chakkarapani
Author: Kerry Woolfall
Author: Samantha Johnson
Author: Patricia Ellen Grant
Author: Sarah Land
Author: Mariam Mahmoud
Author: Tony Brady
Author: Victoria Cornelius
Author: Eleri Adams
Author: Jon Dorling ORCID iD
Author: Narendra Aladangadi
Author: Paul Fleming
Author: Ronit Pressler
Author: Andrew Shennan
Author: Stavros Petrou
Author: Aung Soe
Author: Paul Basset
Author: Seetha Shankaran
Author: Sudhin Thayyil

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